A rare, fatal disorder was corrected in eight newborns by ‘touching their DNA’
The clinical trial In patients with Parkinson’s, melanoma, leukemia, HIV, hemophilia… gene therapy is envisaged as a valid option in more and more diseases. Now, a new clinical trial shows that it could also “safely” correct the immune systems of newborns diagnosed with a rare and life-threatening hereditary disorder: X-linked severe combined immunodeficiency (X-SCID). At…